Gene-Based Therapy Restores Cellular Development and Function in Brain Cells From People With Timothy Syndrome

Gene-Based Therapy Restores Cellular Development and Function in Brain Cells From People With Timothy Syndrome

NIH-supported analyze shows potential remedy pathway for neurodevelopmental ailment April 24, 2024 • Press Release In a proof-of-principle analyze, scientists shown the functionality of a chance new therapy for Timothy syndrome , an generally existence-threatening and uncommon genetic situation that has Read More